News & Analysis as of

Regenerative Medicine

Goodwin

Intellia Initiates Rolling BLA Submission for In Vivo CRISPR Therapy in Hereditary Angioedema

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On April 27, 2026, Intellia Therapeutics (“Intellia”) announced that it has begun a rolling submission of a biologics license application (BLA) to the FDA for lonvoguran ziclumeran (lonvo-z), an investigational therapy for...more

Hogan Lovells

FDA issues guidance on “plausible mechanism” approvals, declares single pivotal trials with confirmatory evidence as new default...

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On Monday, the U.S. Food and Drug Administration (FDA) published draft guidance formalizing a “plausible mechanism” approval framework for individualized therapies, particularly genome editing and RNA-based products. Although...more

Ropes & Gray LLP

NIH Prohibits Use of Federal Funds for Research Involving Human Fetal Tissue from Elective Abortions

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On January 22, 2026, the National Institutes of Health (NIH) issued NOT-OD-26-028, prohibiting the use of NIH funds for research involving human fetal tissue (HFT) obtained from elective abortions (the Notice)....more

Bergeson & Campbell, P.C.

EC Releases Proposed Biotech Act

On December 15, 2025, the European Commission (EC) announced a legislative package that includes a proposal for a regulation to establish measures to strengthen the European Union’s (EU) biotechnology and biomanufacturing...more

Troutman Pepper Locke

Iowa AG Obtains Court Injunction and Civil Penalties Against Stem Cell Company in Four-Day Trial

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After a four-day trial, Iowa Attorney General (AG) Brenna Bird obtained a ruling and judgment against Omaha-based stem cell businesses and its owner/CEO for deceptively marketing “regenerative medicine” stem cell injections...more

Ropes & Gray LLP

Rare Disease Focus: FDA’s Trio of Cell and Gene Therapy Draft Guidances Highlight Expedited Programs, Innovative Trial Designs,...

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FDA’s Center for Biologics Evaluation and Research (“CBER”) recently issued a trio of new draft guidances to assist sponsors who are developing and conducting postapproval studies of cell and gene therapies (“CGTs”):...more

Hogan Lovells

How to Negotiate Cell & Gene Therapy Contracts with German Treatment Centers - Trends in Cell, Tissue, and Gene Therapies

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For autologous cell and gene therapies (CGTs), the collection of patients‘ cells is the first step in the manufacture of the medicinal product. In Germany, this step is usually conducted by specialized treatment centers that...more

Fuerst Ittleman David & Joseph

Florida's New Stem Cell Laws: Unburdened by What Has Been

On July 1, 2025, Florida’s new “Stem Cell Therapy” legislation became effective, adding Fla.Stat. § 458.3245 to Florida’s Medical Practices statutes and § 459.0127 to Florida’s Osteopathic Medicine statutes. Florida’s new...more

Sheppard

What to Watch: Human Cell and Tissue Product Regulation

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Since the year began, we have attempted to divine the new administration’s approach to regulating human cell and tissue products (“HCT/Ps”). What we have found is a collection of seemingly contradictory signals, keeping us...more

Wilson Sonsini Goodrich & Rosati

FDA Releases Three Draft Guidances to Facilitate Development of Cell and Gene Therapies

Key Takeaways - - The U.S. Food and Drug Administration (FDA) recently issued three draft guidances concerning development of cell and gene therapy (CGT) products. The guidances provide advice concerning qualifying CGTs...more

Sheppard

FDA Touts Continued Commitment to Cell and Gene Therapy Products Through Trio of Guidances

Sheppard on

In late September, the U.S. Food & Drug Administration (“FDA”) issued three draft guidances related to cell and gene therapy (“CGT”) products: (1) Innovative Designs for Clinical Trials of CGT Products in Small Populations...more

Holland & Knight LLP

FDA Publishes New Draft Guidance on Regenerative Medicine Therapies

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The U.S. Food and Drug Administration (FDA) on Sept. 20, 2025, issued draft guidance, "Expedited Programs for Regenerative Medicine Therapies for Serious Conditions," outlining how sponsors can utilize FDA's expedited review...more

Hogan Lovells

Cell & gene therapy clinical trials, development promoted in three new FDA guidance documents - Trends in Cell, Tissue, and Gene...

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On Wednesday, the U.S. Food and Drug Administration (FDA) published three new draft guidances that aim to offer greater clarity to sponsors of cell and gene therapies (CGTs) on issues related to clinical trial design,...more

Hogan Lovells

Japan’s conditional approval pathway offers regenerative medicines earlier market access - Trends in Cell, Tissue, and Gene...

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Japan continues to position itself as a global leader in regenerative medicine through its progressive regulatory framework tailored to the unique characteristics of cell, tissue, and gene therapy (CTGT) products....more

Ropes & Gray LLP

Stem Cell Litigation Update: FDA Won the Latest Battle, but the Future of HCT/P Enforcement Remains Unclear

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On September 27, 2024, the U.S. Court of Appeals for the Ninth Circuit reversed the district court’s decision in U.S. v. California Stem Cell Treatment Center, Inc. (“California Stem Cell”), holding that a clinic’s stem cell...more

Foley & Lardner LLP

USC Announces Stem Cell Collaboration

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Treatment and prevention of heart failure are unmet medical needs in the United States. One in every eight deaths in the United States can be linked to this disease. The Keck School of Medicine at USC and the biotechnology...more

Knobbe Martens

FDA Approves Colony Stimulating Factor-1 Receptor (Csf-1R) Blocking Antibody for Treatment of Chronic Graft-Versus-Host Disease...

Knobbe Martens on

On August 14, 2024, the U.S. Food and Drug Administration (FDA) approved a colony stimulating factor-1 receptor (CSF-1R)-blocking antibody, NIKTIMVO (axatilimab-csfr) developed by Incyte Corporation (and in-licensed from...more

Napoli Shkolnik

The Risks of Unregulated Regenerative Medicine

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A recent New York Times article reported that dozens of spine surgery patients at NewYork-Presbyterian/Weill Cornell Medical Center were treated with a product that was not approved for use in such procedures. Burst...more

Hogan Lovells

O.K. Corral: FDA sets stage to appeal California Stem Cell Treatment Center decision

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Last year, a federal court in California ruled against the U.S. Food and Drug Administration (FDA) in a matter where the government alleged that a stem cell clinic’s products should be regulated as new drugs. The decision...more

Hogan Lovells

Six strategies for clinical trial & marketing application success as FDA requires HCT/P BLAs

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Now that FDA’s grace period for regenerative medicines has ended, many manufacturers of human cell, tissue, or cellular- or tissue-based products (HCT/Ps) will be required to file a biologics license application (BLA) with...more

Hogan Lovells

CMS proposes sweeping changes to regenerative medicine reimbursement framework

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Last month, the Centers for Medicare & Medicaid Services (CMS) released new and significant proposals impacting Medicare coding, coverage, and reimbursement for a class of regenerative medicines known as “skin substitutes,” a...more

Hogan Lovells

World Stem Cell Summit panel compares global trends in regenerative medicine regulations

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Speaking at the World Stem Cell Summit hosted by the Regenerative Medicine Foundation, Hogan Lovells partners Mike Druckman, Ernesto Algaba, Mandi Jacobson, Lu Zhou, Mikael Salmela, Charlotte Damiano, and Lowell Zeta, along...more

Hogan Lovells

World Stem Cell Summit panel cautions over stepped up HCT/P enforcement, reimbursement issues

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Speaking at the World Stem Cell Summit hosted by the Regenerative Medicine Foundation last week, Hogan Lovells partners Mike Druckman, Stuart Langbein, and Thomas Beimers discussed evolving government reimbursement issues for...more

Hogan Lovells

FDA invites comments on xenotransplantation product regulatory standards ahead of public meeting

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On June 29-30, 2022, the U.S. Food and Drug Administration (FDA) will hold a virtual public meeting of the Cellular, Tissue, and Gene Therapies Advisory Committee (CTGTAC) to discuss its regulatory expectations for...more

Hogan Lovells

Time’s really up! FDA authority to crack down on regenerative medicines upheld as grace period ends

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On July 9, 2021, the U.S. Food and Drug Administration’s Center for Biologics Evaluation and Research (CBER) added a Q&A page on its website about the May 31 end of the grace period intended to provide developers of human...more

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